Kim Smith-Whitley, MD—director of the Comprehensive Sickle Cell Center at Children’s Hospital of Philadelphia—shares why her PCORI-funded project is focused on improving the quality of life for young adults with sickle cell disease who are transitioning from pediatric-focused care to adult-focused care.
Monday, March 2, 2020; 2:30 p.m. - 7:30 p.m. ET
Wednesday, April 1, 2020; 5:00 p.m. ET
Learn about the more than two dozen PCORI-funded projects that seek to help patients with rare diseases—affecting fewer than 200,000 people, such as sickle cell disease and lupus nephritis—and those who care for them make better-informed decisions about their treatment.
Doug Lindsay, who spent 11 years home- and bed-bound due to a developing rare disease, outlines the journey he led with his doctors to develop the right treatment and cure.
Join us via webinar or in person when the Board will vote on funding for new research awards and awards to disseminate PCORI-funded research results, and consider three new PCORI Funding Announcements.
PCORI's Horizon Scanning System can also help us discover and better understand future topic areas for patient-centered comparative effectiveness research.